h*****g
发帖数: 42 | 1 国内朋友的小孩得了黏多糖症(4型)，现在世界上还没有可用的药。BioMarin公司已经
开发了针对黏多糖6型的药，现在针对黏多糖4型的药正在进行三期临床试验。这边有在
BioMarin公司工作的兄弟姐妹吗？能否帮忙打听下公司内招募病人都如何操作的？他们
的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去，心如刀割啊！
先行谢过各位好心人！ |
h*****g
发帖数: 42 | 2 自己先顶一下。
【在 h*****g 的大作中提到】
: 国内朋友的小孩得了黏多糖症(4型)，现在世界上还没有可用的药。BioMarin公司已经
: 开发了针对黏多糖6型的药，现在针对黏多糖4型的药正在进行三期临床试验。这边有在
: BioMarin公司工作的兄弟姐妹吗？能否帮忙打听下公司内招募病人都如何操作的？他们
: 的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去，心如刀割啊！
: 先行谢过各位好心人！
|
u**l
发帖数: 1043 | 3 I have a friend there and I will help you ask her.
【在 h*****g 的大作中提到】
: 自己先顶一下。
|
h*****g
发帖数: 42 | 4 太好了，谢谢谢谢！
【在 u**l 的大作中提到】
: I have a friend there and I will help you ask her.
|
j*****u
发帖数: 446 | 5 http://clinicaltrials.gov/
find all clinical trails from here. hope it helps.
【在 h*****g 的大作中提到】
: 国内朋友的小孩得了黏多糖症(4型)，现在世界上还没有可用的药。BioMarin公司已经
: 开发了针对黏多糖6型的药，现在针对黏多糖4型的药正在进行三期临床试验。这边有在
: BioMarin公司工作的兄弟姐妹吗？能否帮忙打听下公司内招募病人都如何操作的？他们
: 的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去，心如刀割啊！
: 先行谢过各位好心人！
|
h*****g
发帖数: 42 | 6 Judyzhu,谢谢你！
【在 j*****u 的大作中提到】
: http://clinicaltrials.gov/
: find all clinical trails from here. hope it helps.
|
w********o
发帖数: 1621 | 7 Didn't expect to see BioMarin on this board.
In order to be enrolled into their studies, you need go to participating
sites and asked to be evaluated. If you meet all the inclusion/exclusion
criteria, then you will be enrolled. To find out which sites are currently
screening patients, you can go to BioMarin's website or call them.
Before you get the kids to US to see those investigators, you better get a
clear idea what their screening criteria is by checking the inclusion/
exclusion details on www.clinicaltrials.gov.
If it's a randomized, blinded and controlled study, even if the kid is
enrolled, there is still a chance to be assigned to placebo group.
Good luck. |
h*****g
发帖数: 42 | 8 Thanks for your reminder. I went through the inclusion/exclusion criteria on
their trial website, it's a randomized and double-blind study.
【在 w********o 的大作中提到】
: Didn't expect to see BioMarin on this board.
: In order to be enrolled into their studies, you need go to participating
: sites and asked to be evaluated. If you meet all the inclusion/exclusion
: criteria, then you will be enrolled. To find out which sites are currently
: screening patients, you can go to BioMarin's website or call them.
: Before you get the kids to US to see those investigators, you better get a
: clear idea what their screening criteria is by checking the inclusion/
: exclusion details on www.clinicaltrials.gov.
: If it's a randomized, blinded and controlled study, even if the kid is
: enrolled, there is still a chance to be assigned to placebo group.
|
M*****R
发帖数: 650 | 9 Just asked. They are doing clinical trial on this, but probably not in China
. Not sure how this can work out.
Anyway, check your mitbbs mail for contact info.
【在 h*****g 的大作中提到】
: 国内朋友的小孩得了黏多糖症(4型)，现在世界上还没有可用的药。BioMarin公司已经
: 开发了针对黏多糖6型的药，现在针对黏多糖4型的药正在进行三期临床试验。这边有在
: BioMarin公司工作的兄弟姐妹吗？能否帮忙打听下公司内招募病人都如何操作的？他们
: 的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去，心如刀割啊！
: 先行谢过各位好心人！
|
